Xagena Medicina

Rare diseases by Xagena


RareDiseasesNews.net - Rare diseaseRare diseases, Orphan drugs, Rare disease, Rare disease Xagena, Xagena Medical News, Rare syndrome, Rare neurological disorders, Orphan drug,  RareDiseasesNews.net - Rare ...RareDiseasesNews.net - Rare diseases Xagena ... Late-onset ...Rett syndromeRett syndrome is a neurodevelopmental disorder ...Plerixafor targets specific ...Plerixafor targets specific defect causing WHIM syndrome. A ...Alagille syndromeNOTCH2 mutations gene found for Alagille syndrome may be ...BronchiectasisFDA OOPD: orphan drug designation for Erdosteine in ...Vitamin B12 deficiencyDiscovered a mutation that causes a rare, inherited vitamin B12 ...Fanconi anemiaFanconi anemia ( FA ) is a rare genetic disorder which affects ...Hepatic porphyriaVariegate porphyria ( VP ) is an autosomal dominantly inherited ...Prader-Willi syndromePrader-Willi syndrome is a rare genetic disorder which affects ...Aplastic anemiaA comparison clinical study of two aplastic anemia treatments ...